Resamirigene bilparvovec
id:
resamirigene-bilparvovec-244-6927897
title:
Resamirigene bilparvovec
text:
Resamirigene bilparvovec is an experimental gene therapy medication studied as a treatment for X-linked myotubular myopathy (XLMTM), a severe and usually fatal genetic disorder affecting mainly male infants and caused by a mutation in the MTM1 gene. The drug consists of a MTM1 transgene encapsulated in a viral vector from the adeno-associated virus class (AAV8) and is administered to affected children as an intravenous infusion. The treatment is being developed by Astellas Gene Therapies and is
brand slug:
wiki
category slug:
encyclopedia
description:
Experimental treatment for X-linked myotubular myopathy
original url:
https://en.wikipedia.org/wiki/Resamirigene_bilparvovec
date created:
date modified:
2023-12-05T04:45:30Z
main entity:
{"identifier":"Q108910814","url":"https://www.wikidata.org/entity/Q108910814"}
image:
fields total:
13
integrity:
14