Gene therapy of the human retina
id:
gene-therapy-of-the-human-retina-267-17495478
title:
Gene therapy of the human retina
text:
Retinal gene therapy holds a promise in treating different forms of non-inherited and inherited blindness. In 2008, three independent research groups reported that patients with the rare genetic retinal disease Leber's congenital amaurosis had been successfully treated using gene therapy with adeno-associated virus (AAV). In all three studies, an AAV vector was used to deliver a functional copy of the RPE65 gene, which restored vision in children suffering from LCA. These results were widely see
brand slug:
wiki
category slug:
encyclopedia
description:
original url:
https://en.wikipedia.org/wiki/Gene_therapy_of_the_human_retina
date created:
date modified:
2023-12-18T05:18:10Z
main entity:
{"identifier":"Q4682229","url":"https://www.wikidata.org/entity/Q4682229"}
image:
fields total:
13
integrity:
13