Branaplam

id: branaplam-163-3231591
title: Branaplam
text: Branaplam is a pyridazine derivative that is being studied as an experimental drug. It was originally developed by Novartis to treat spinal muscular atrophy (SMA); since 2020 it was being developed to treat Huntington's disease but the trial ended in 2023 due to toxicity concerns. As a treatment for SMA, branaplam increases the amount of functional survival of motor neuron protein produced by the SMN2 gene through modifying its splicing pattern. It was studied since 2014 in a clinical trial in c
brand slug: wiki
category slug: encyclopedia
description: Chemical compound
original url: https://en.wikipedia.org/wiki/Branaplam
date created: 2017-03-10T13:07:14Z
date modified: 2024-08-28T11:55:24Z
main entity: {"identifier":"Q27285985","url":"https://www.wikidata.org/entity/Q27285985"}
image: {"content_url":"https://upload.wikimedia.org/wikipedia/commons/9/9b/Branaplam_skeletal.svg","width":512,"height":230}
fields total: 13
integrity: 16

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